Adeno-associated viral vector serotype 8 containing a functional copy of
the codon-optimised F8 cDNA encoding the B-domain deleted human
coagulation factor VIII |
Treatment of haemophilia A |
EU/3/18/2015 |
Adeno-associated viral vector serotype 5 containing a B-domain deleted
variant of human coagulation factor VIII gene |
Treatment of haemophilia
A |
EU/3/16/1622 |
Recombinant adeno-associated viral vector containing a bioengineered
capsid and a codon-optimised expression cassette to drive the expression
of the SQ form of a B-domain deleted human coagulation factor VIII |
Treatment of haemophilia A |
EU/3/18/2079 |
Recombinant adeno-associated viral vector serotype 6 encoding the
B-domain-deleted human factor VIII |
Treatment of haemophilia A |
EU/3/17/1874 |
Adeno-associated viral vector serotype rh10 containing the human factor
IX gene for the treatment of haemophilia B- |
Treatment of haemophilia B |
EU/3/15/1599 |
Fidanacogene elaparvovec |
Treatment of haemophilia B |
EU/3/18/2090 |
Lentiviral vector encoding human coagulation factor IX |
Treatment of
haemophilia B |
EU/3/19/2141 |
Adeno-associated viral vector containing the human factor-IX gene |
Treatment of haemophilia B |
EU/3/11/938 |
Recombinant adeno-associated viral vector containing a codon-optimized
Padua derivative of human coagulation factor IX cDNA |
Treatment of
haemophilia B |
EU/3/18/1999 |
Recombinant adeno-associated viral vector serotype S3 containing
codon-optimised expression cassette encoding human coagulation factor IX
variant |
Treatment of haemophilia B |
EU/3/18/2080 |