CLINICAL DATA
CLINICAL DATA
CLINICAL DATA
CLINICAL DATA
CLINICAL DATA
CLINICAL DATA
CLINICAL DATA
EXPANSION SIZE EXPANSION SIZE
FOCI ANALYSIS
FOCI ANALYSIS
FOCI ANALYSIS
FOCI ANALYSIS
FOCI ANALYSIS
Patient
Age of onset
Age at sampling
Gender
mRS
MIRS
Biceps MRC
6MWT
Muscle
Myoblasts
No. of cells studied
% cells with foci
Mean
Median
Range
P1
15*
36
F
2
4
4
348
691
823
72
97,2%
2,3
2
0-6
P2
48
54
M
2
3
5
251
ND
ND
72
98,6%
2,6
2
0-7
P3
36
41
F
1
2
5
368
208
1686
63
81%
1,4
1
0-4
P4
27
39
F
4
4
4
NP
469
561
39
97,4%
2,7
3
0-5
P5
36
41
M
2
3
5
519
135
150
66
28,8%
0,6
0
0-7