Targeted busulfan-based conditioning unrelated donor bone marrow transplantation for Diamond-Blackfan anemia
Katsuhide Eguchi1), Masataka Ishimura1), Akihiro Tamura2), Nobuhiro Ito3), Naoki Hirano4), Shunichi Adachi1), Keishiro Kinoshita1), Hirokazu Kobushi1), Yutaro Yada1), Motoshi Sonoda1), Akira Shiraishi1), Yoshiyuki Kosaka2), Kiminori Terui5), Etsuro Ito5), Shouichi Ohga1)
Affiliations : 1. Department of Pediatrics, Graduate School of Medical Sciences, Kyushu University, Fukuoka, Japan, 2. Department of Hematology and Oncology, Kobe Children’s Hospital, Hyogo, Japan, 3. Department of Pediatrics, Nagasaki University Hospital, Nagasaki, Japan, 4. Department of Pediatrics, Oita University Faculty of Medicine, Oita, Japan, 5. Department of Pediatrics, Hirosaki University Graduate School of Medicine, Aomori, Japan.
Corresponding author : Masataka Ishimura, Department of Pediatrics, Graduate School of Medical Sciences, Kyushu University, 3-1-1 Maidashi, Higashi-ku, Fukuoka, 812-8582, Japan. PHONE: +81-92-642-5421, FAX: +81-92-642-5435, E-mail: ischii@pediatr.med.kyushu-u.ac.jp
Word count  unstructured abstract: 100 words (< 100), text: 1191 words (< 1200)
Number of tables and figures  TABLE: 1, Figure: 1 (up to 2), References: 20 (as needed)
Short running title: Targeted BU-conditioning unrelated BMT for DBA
Keywords: Diamond-Blackfan anemia; targeted busulfan; post-transplant neoplasms