Targeted busulfan-based
conditioning unrelated donor bone marrow transplantation for
Diamond-Blackfan anemia
Katsuhide Eguchi1), Masataka
Ishimura1),
Akihiro
Tamura2), Nobuhiro Ito3), Naoki
Hirano4), Shunichi Adachi1),
Keishiro Kinoshita1), Hirokazu
Kobushi1), Yutaro Yada1), Motoshi
Sonoda1), Akira Shiraishi1),
Yoshiyuki Kosaka2), Kiminori
Terui5), Etsuro Ito5), Shouichi
Ohga1)
Affiliations : 1. Department of Pediatrics, Graduate School of
Medical Sciences, Kyushu University, Fukuoka, Japan, 2. Department of
Hematology and Oncology,
Kobe
Children’s Hospital, Hyogo, Japan, 3. Department of Pediatrics, Nagasaki
University Hospital, Nagasaki, Japan, 4. Department of Pediatrics, Oita
University Faculty of Medicine, Oita, Japan, 5. Department of
Pediatrics, Hirosaki University Graduate School of Medicine, Aomori,
Japan.
Corresponding author : Masataka Ishimura, Department of
Pediatrics, Graduate School of Medical Sciences, Kyushu University,
3-1-1 Maidashi, Higashi-ku, Fukuoka, 812-8582, Japan. PHONE:
+81-92-642-5421, FAX: +81-92-642-5435, E-mail:
ischii@pediatr.med.kyushu-u.ac.jp
Word count unstructured abstract: 100 words
(< 100), text: 1191 words
(< 1200)
Number of tables and figures TABLE: 1, Figure: 1 (up to 2),
References: 20 (as needed)
Short running title: Targeted BU-conditioning unrelated BMT for
DBA
Keywords: Diamond-Blackfan anemia; targeted busulfan;
post-transplant neoplasms